Showing 4140 results for "als"

Columbia gets $15M to design gene therapies for rare ALS forms

Columbia University researchers will use a $15 million federal grant to design individualized gene therapies for nine people with ultra-rare genetic forms of amyotrophic lateral sclerosis (ALS). The three-year grant comes from the National Institute of Neurological Disorders and Stroke’s (NINDS) Ultra-rare Gene-based Therapy (URGenT) Network, a program…

Relyvrio (sodium phenylbutyrate and taurursodiol) for ALS

Relyvrio (sodium phenylbutyrate and taurursodiol) is an oral treatment approved in the U.S. and Canada to help slow disease progression in adults with amyotrophic lateral sclerosis (ALS). The therapy has been shown in clinical trials to reduce functional decline and to significantly extend patient survival.