At-home Music Therapy Program May Help Bulbar-onset Patients
An at-home music therapy program aimed at improving speech, swallowing, and respiration in people with amyotrophic lateral sclerosis (ALS)…
Articles by Lindsey Shapiro, PhD
FDA Grants Orphan Drug Status to TQS-168 for ALS Treatment
The U.S. Food and Drug Administration has granted orphan drug designation to Tranquis Therapeutics‘ experimental therapy TQS-168 for…
Nearly 25K Were Living With ALS in 2017, US Registry Estimates
The estimated 2017 U.S. prevalence of individuals with amyotrophic lateral sclerosis (ALS) was 24,821, or 7.7 per 100,000 people,…
Researchers Develop New Tool to Aid in Rare Disease Gene Discovery
A research team has developed a new way to search for genes and gene mutations that may contribute to the…
ALS Researcher Winner of Inaugural Target ALS Luker Courage Award
Merit E. Cudkowicz, MD,  is the winner of the inaugural Target ALS Rebecca Luker Courage Award in recognition…
Mutations in 22 Genes Linked to Sporadic ALS in Large Group Study
Note: Frontiers in Genetics, the publisher of the study discussed in this ALS News Today news story, received a request…
Job-related Lead Exposure Linked to Shorter Survival After Diagnosis
Occupational exposure to lead — a heavy metal — prior to disease onset is associated with a more severe disease…
Blocking Astrocyte Protein May Slow ALS Progression, Study Finds
Blocking channels containing the connexin 43 (Cx43) protein on astrocytes — a type of nerve support cell — slowed disease…
Dosing Begins in Phase 1 Trial of PrimeC, Combo Therapy for ALS
A first healthy volunteer has been enrolled in a Phase 1 trial and given a first dose of PrimeC,…
Progranulin Gene Therapy Shows Promise in Preclinical Studies
ALPHA-0602, an investigational gene therapy for amyotrophic lateral sclerosis (ALS), can successfully increase progranulin levels and reduce the toxicity…